Synonyms: (+)-(R)-N-[2-Hydroxy-3-(1-piperidinyl)propoxy]pyridine-1-oxide-3-carboximidoyl chloride, maleate salt; (R)-3-(Chloro(2-hydroxy-3-(piperidin-1-yl)propoxyimino)methyl)pyridine 1-oxide, maleate salt; Anti-neurodegeneration agent 1; BRX 220; BRX-220; BRX220; N-[(2R)-2-Hydroxy-3-(1-piperidinyl)propoxy]-3-pyridinecarboximidoyl chloride 1-oxide, maleate salt; maleate salt
Molecular Formula: C14H20ClN3O3 · C4H4O4
Molecular Weight: 429.85
Linear Structural Formula: C14H20ClN3O3 · C4H4O4
MDL Number: MFCD28143527
Purity: >=98% (HPLC)
Storage: 2-8C
Biochem Physiol Actions: Arimoclomol is an orally available, CNS-penetrant coinducer of heat shock proteins (HSPs), notably HSP70, that exhibits in vivo efficay in disease models of diabetes, Gaucher disease (GD), sporadic inclusion body myositis (sIBM), and neurological disorders, including amyotrophic lateral sclerosis (ALS) and Niemann-Pick disease type C1 (NPC1). Note: arimoclomol maleate and citrate salt forms are known as BRX-220 and BRX-345, respectively.